New Collaborative Study: Gene Therapy for AMN

29th October 2018

A major step forward towards gene therapy for the spinal cord form of adrenoleukodystrophy (AMN) via AAV mediated gene correction of the spinal cord. A collaborative study by Harvard Medical School and the Academic Medical Centre at the University of Amsterdam has recently been published in Human Gene Therapy; read it here.


17 hours ago

ALD Life

We are delighted to announce that on the 15th May 2019 ALD Life will become Alex, The Leukodystrophy Charity (Alex TLC), able to support people with all Leukodystrophies, where no other support is available.

We’ll still be providing people with ALD and AMN the high-quality information, support, services and networks they already expect from us, but we want to help people with similar conditions and their families to have access to these too.

We will be sharing more information about the launch in the coming weeks, so stay tuned!

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